Adults who have transfusion dependent thalassaemia are being given access to stem cell transplantations on the NHS, a treatment previously available only to children.
Advances in transplant treatment, such as better drugs to manage a patient before, during, and after transplantation, mean that allogeneic haematopoietic stem cell transplant (HSCT) has been recommended for eligible adults over 18 in new guidance from NHS England’s clinical priorities advisory group.
Transfusion dependent thalassaemia is a severe form of the condition, …